tara

tara
LA Mayor's Office Acknowledges the NDF's Advocacy with GNEM

Thursday, July 12, 2012

New Gene Transfer shows Promise for Limb Girdle and other Muscular Dystrophies

When I was misdiagnosed and placed in the Limb Girdle muscular dystrophy category, I was hoping that the gene therapy the researchers were trying  at the time would be successfull.  This article just released shows how far gene therapy has come and I think  there is great hope for people with HIBM.  I have attached the link of the complete article.

"The challenge of treating patients with genetic disorders in which a single mutated gene is simply too large to be replaced using traditional gene therapy techniques may soon be a thing of the past. A Nationwide Children's Hospital study describes a new gene therapy approach capable of delivering full-length versions of large genes and improving skeletal muscle function. The strategy may hold new hope for treating dysferlinopathies and other muscular dystrophies".


http://www.labspaces.net/121546/New_gene_transfer_strategy_shows_promise_for_limb_girdle_and_other_muscular_dystrophies

1 comment:

Anonymous said...

Hi Tara,

How do I become a follower of your blog?

Kristine